My research interest lies in the field of gene therapy for treatment of inherited diseases and cellular immunotherapy to treat pediatric oncology patients. For treatment of pediatric malignancies, in particular acute myeloid leukemia and neuroblastoma, cord-blood derived cells are developed to create dendritic cell vaccines and T cell receptor and chimeric antigen receptor T cell therapies as adjuvant therapies after hematopoietic cell transplantation or to produce off-the-shelf drug products. Additionally, I work on hematopoietic stem cell gene therapy to treat lysosomal storage diseases, such as Pompe disease, which is a neuromuscular disorder. We use cutting-edge technologies including lentiviral vectors, adeno associated viral vectors and genome-editing applications in our drug products to test in preclinical efficacy and safety studies.